Recombination-activating gene 1 (Rag1)-deficient mice with severe combined immunodeficiency treated with lentiviral gene therapy demonstrate autoimmune Omenn-like syndrome

Recombination-activating gene 1 (Rag1)-deficient mice with severe combined immunodeficiency treated with lentiviral gene therapy demonstrate autoimmune Omenn-like syndrome / van Til, N.p., Sarwari, R., Visser, T.p., Hauer, J., Lagresle Peyrou, C., van der Velden, G., Malshetty, V., Cortes, P., Jollet, A., Danos, O., Cassani, B., Zhang, F., Thrasher, A.j., Fontana, E., Poliani, P.L., Cavazzana, M., Verstegen, M.m., Villa, A., Wagemaker, G.. - In: JOURNAL OF ALLERGY AND CLINICAL IMMUNOLOGY. - ISSN 0091-6749. - 133:4(2014), pp. 1116-1123. [10.1016/j.jaci.2013.10.009]