Therapeutic advantages of combined gene/cell therapy strategies in a murine model of {GM}2 gangliosidosis

Therapeutic advantages of combined gene/cell therapy strategies in a murine model of {GM}2 gangliosidosis / Sala, D., Ornaghi, F., Morena, F., Argentati, C., Valsecchi, M., Alberizzi, V., Di Guardo, R., Bolino, A., Aureli, M., Martino, S., Gritti, A.. - In: MOLECULAR THERAPY. METHODS & CLINICAL DEVELOPMENT. - ISSN 2329-0501. - 25:(2022), pp. 170-189. [10.1016/j.omtm.2022.03.011]