Access to gene therapy for rare diseases when commercialization is not fit for purpose

Access to gene therapy for rare diseases when commercialization is not fit for purpose / Fox, T., Bueren, J., Candotti, F., Fischer, A., Aiuti, A., Lankester, A., Albert, M., Bernardo, M.E., Cavazzana, M., Ehl, S., Neven, B., Prevot, J., Schambach, A., Sevilla, J., Thrasher, A., Wynn, R., Booth, C.. - In: NATURE MEDICINE. - ISSN 1078-8956. - 29:3(2023), pp. 518-519. [10.1038/s41591-023-02208-8]