A direct gene transfer strategy via brain internal capsule reverses the biochemical defect in Tay-Sachs disease
Academic Article
Publication Date:
2005
Iris type:
1.1 Articolo in rivista
List of contributors:
Martino, S.; Marconi, P.; Tancini, B.; Dolcetta, D.; CUSELLA DE ANGELIS, M. G.; Montanucci, P.; Bregola, G.; Sandhoff, K.; Bordignon, Claudio; Emiliani, C.; Manservigi, R.; AND A., Orlacchio
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