Use of Defibrotide to help prevent post-transplant endothelial injury in a genetically predisposed infant with metachromatic leukodystrophy undergoing hematopoietic stem cell gene therapy

Articolo

Data di Pubblicazione:

2018

Citazione:

Use of Defibrotide to help prevent post-transplant endothelial injury in a genetically predisposed infant with metachromatic leukodystrophy undergoing hematopoietic stem cell gene therapy / Calbi, Valeria; Fumagalli, Francesca; Consiglieri, Giulia; Penati, Rachele; Acquati, Serena; Redaelli, Daniela; Attanasio, Vanessa; Marcella, Facchini; Cicalese, Maria Pia; Migliavacca, Maddalena; Barzaghi, Federica; Ferrua, Francesca; Assanelli, Andrea; Silvani, Paolo; Zoccolillo, Matteo; Chidini, Giovanna; Chiesa, Robert; Arora, Ruchi; Ciotti, Francesca; Sarzana, Marina; Antonioli, Gigliola; Baldoli, Cristina; Morena, Francesco; Martino, Sabata; Ardissino, Gian Luigi; Sora, Maria Grazia Natali; Naldini, Luigi; Ciceri, Fabio; Aiuti, Alessandro; Bernardo, Maria Ester. - In: BONE MARROW TRANSPLANTATION. - ISSN 0268-3369. - 53:7(2018), pp. 913-917. [10.1038/s41409-017-0085-1]

Tipologia CRIS:

1.1 Articolo in rivista

Keywords:

Genetic Therapy; Hematopoietic Stem Cell Transplantation; Humans; Leukodystrophy, Metachromatic; Male; Platelet Aggregation Inhibitors; Polydeoxyribonucleotides; Transplantation Conditioning; Twins

Elenco autori: