Minicircle DNA-based Gene Therapy Coupled With Immune Modulation Permits Long-term Expression of alpha-L-Iduronidase in Mice With Mucopolysaccharidosis Type I
Academic Article
Publication Date:
2011
Iris type:
1.1 Articolo in rivista
List of contributors:
Osborn, Mj; Mcelmurry, Rt; Lees, Cj; Defeo, Ap; Chen, Zy; Kay, Ma; Naldini, Luigi; Freeman, G; Tolar, J; Blazar, Br
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