Direct Intra-Brain LV-Mediated Gene Delivery Leads to Widespread Transgene Distribution and High-Level Enzymatic Correction in the Whole CNS of Twitcher Mice

Direct Intra-Brain LV-Mediated Gene Delivery Leads to Widespread Transgene Distribution and High-Level Enzymatic Correction in the Whole CNS of Twitcher Mice / Lattanzi, A; Maderna, C; Amendola, M; Sergi, Ls; Conti, D; Martino, S; Naldini, L; Gritti, A. - In: MOLECULAR THERAPY. - ISSN 1525-0016. - (2009).