Early sulfatide storage and progressive neuronal and glial cell dysfunction revealed by human iPSC-based models of metachromatic leukodystrophy are rescued by lentiviral-mediated restoration of ARSA activity

Abstract

Data di Pubblicazione:

2017

Citazione:

Early sulfatide storage and progressive neuronal and glial cell dysfunction revealed by human iPSC-based models of metachromatic leukodystrophy are rescued by lentiviral-mediated restoration of ARSA activity / Frati, ., G, ., Luciani, ., M, ., Meneghini, ., V, ., De, C., S, ., Stahlman, ., M, ., Grossi, ., S, ., Morena, ., F, ., Blomqvist, ., M, ., Filocamo, ., M, ., Martino, ., S, ., et al.. - In: HUMAN GENE THERAPY. - ISSN 1043-0342. - (2017).

Tipologia CRIS:

1.5 Abstract in rivista

Elenco autori:

Frati, ; G, ; Luciani, ; M, ; Meneghini, ; V, ; De, Cicco; S, ; Stahlman, ; M, ; Grossi, ; S, ; Morena, ; F, ; Blomqvist, ; M, ; Filocamo, ; M, ; Martino, ; S, ; Gritti, A

Autori di Ateneo:

GRITTI ANGELA

Link alla scheda completa:

https://iris.unisr.it/handle/20.500.11768/160272

Pubblicato in:

HUMAN GENE THERAPY

Journal