Long-term natural history data in Duchenne muscular dystrophy ambulant patients with mutations amenable to skip exons 44, 45, 51 and 53

Long-term natural history data in Duchenne muscular dystrophy ambulant patients with mutations amenable to skip exons 44, 45, 51 and 53 / Brogna, C; Coratti, G; Pane, M; Ricotti, V; Messina, S; D'Amico, A; Bruno, C; Vita, G; Berardinelli, A; Mazzone, E; Magri, F; Ricci, F; Mongini, T; Battini, R; Bello, L; Pegoraro, E; Baranello, G; Previtali, S; Politano, L; Comi, Gp; Sansone, Va; Donati, A; Bertini, E; Muntoni, F; Goemans, N; Mercuri, E. - In: PLOS ONE. - ISSN 1932-6203. - 14:6(2018). [10.1371/journal.pone.0218683.]