Therapeutic Efficacy of Hematopoietic Stem Cell Gene Therapy for Hurler Type 1 Mucopolysaccharidosis
Abstract
Publication Date:
2009
Iris type:
4.2 Abstract in Atti di convegno
List of contributors:
Visigalli, I; Delai, S; Stok, M; Cesani, M; Plati, T; Politi, Ls; Di Natale, P; Latini, R; Staszewski, Li; Brambilla, R; Quattrini, A; Mariani, E; Cenci, S; Mrak, E; Rubinacci, A; Sanvito, F; Ponzoni, Maurilio; Naldini, L; Biffi, A.
Book title:
American Society of Gene Therapy
Published in: