Preclinical Modeling Highlights the Therapeutic Potential of Hematopoietic Stem Cell Gene Editing for Correction of X-linked Severe Combined Immunodeficiency
Articolo
Data di Pubblicazione:
2017
Citazione:
Preclinical Modeling Highlights the Therapeutic Potential of Hematopoietic Stem Cell Gene Editing for Correction of X-linked Severe Combined Immunodeficiency / Schiroli, G; Ferrari, S; Conway, A; Jacob, A; Capo, V; Albano, L; Plati, T; Castiello, Mc; Sanvito, F; Gennery, Ar; Bovolenta, C; Palchaudhuri, R; Scadden, Dt; Holmes, Mc; Villa, A; Sitia, G; Lombardo, A; Genovese, P; Naldini, L. - In: SCIENCE TRANSLATIONAL MEDICINE. - ISSN 1946-6242. - (2017). [https://doi.org/10.1126/scitranslmed.aan0820]
Tipologia CRIS:
1.1 Articolo in rivista
Elenco autori:
Schiroli, G; Ferrari, S; Conway, A; Jacob, A; Capo, V; Albano, L; Plati, T; Castiello, Mc; Sanvito, F; Gennery, Ar; Bovolenta, C; Palchaudhuri, R; Scadden, Dt; Holmes, Mc; Villa, A; Sitia, G; Lombardo, A; Genovese, P; Naldini, L
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